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Rajendiran V, Devaraju N, Haddad M, Ravi NSam, Panigrahi L, Paul J, Gopalakrishnan C, Wyman S, Ariudainambi K, Mahalingam G, Periyasami Y, Prasad K, George A, Sukumaran D, Gopinathan S, Pai AAnand, Nakamura Y, Balasubramanian P, Ramalingam R, Thangavel S et al..
2024. Base editing of key residues in the BCL11A-XL-specific zinc finger domains derepresses fetal globin expression.. Mol Ther. 32(3):663-677. DOI:10.1016/j.ymthe.2024.01.023.